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Q26830637-4BFB24CF-8633-44AE-99FC-FB8ACF4C6E4E
Q26830637-4BFB24CF-8633-44AE-99FC-FB8ACF4C6E4E
BestRank
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http://www.wikidata.org/entity/statement/Q26830637-4BFB24CF-8633-44AE-99FC-FB8ACF4C6E4E
Antisense mediated splicing modulation for inherited metabolic diseases: challenges for delivery
P2860
Q26830637-4BFB24CF-8633-44AE-99FC-FB8ACF4C6E4E
BestRank
Statement
http://www.wikidata.org/entity/statement/Q26830637-4BFB24CF-8633-44AE-99FC-FB8ACF4C6E4E
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wasDerivedFrom
54466c8dd307cb9b239ace0a7f59e137f805b834
P2860
Eteplirsen for the treatment of Duchenne muscular dystrophy.