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Q28478879-B129F84F-8394-4291-9D32-9283DCE63F16
Q28478879-B129F84F-8394-4291-9D32-9283DCE63F16
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http://www.wikidata.org/entity/statement/Q28478879-B129F84F-8394-4291-9D32-9283DCE63F16
Iminosugar-based inhibitors of glucosylceramide synthase increase brain glycosphingolipids and survival in a mouse model of Sandhoff disease
P2860
Q28478879-B129F84F-8394-4291-9D32-9283DCE63F16
BestRank
Statement
http://www.wikidata.org/entity/statement/Q28478879-B129F84F-8394-4291-9D32-9283DCE63F16
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type
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wasDerivedFrom
85ffad52ad01372caf071d2fad283b5bd5d61017
P2860
Miglustat in late-onset Tay-Sachs disease: a 12-month, randomized, controlled clinical study with 24 months of extended treatment.