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Q28547115-B61BE60F-739A-4830-87D2-0EA763D32F96
Q28547115-B61BE60F-739A-4830-87D2-0EA763D32F96
BestRank
Statement
http://www.wikidata.org/entity/statement/Q28547115-B61BE60F-739A-4830-87D2-0EA763D32F96
Oral Migalastat HCl Leads to Greater Systemic Exposure and Tissue Levels of Active α-Galactosidase A in Fabry Patients when Co-Administered with Infused Agalsidase
P2860
Q28547115-B61BE60F-739A-4830-87D2-0EA763D32F96
BestRank
Statement
http://www.wikidata.org/entity/statement/Q28547115-B61BE60F-739A-4830-87D2-0EA763D32F96
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wasDerivedFrom
5793c7771d8b37d165b60678687c852527bb901c
P2860
Pharmacological chaperone corrects lysosomal storage in Fabry disease caused by trafficking-incompetent variants.