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Q30496514-07EE411F-D3E8-469E-B113-C034576EDF48
Q30496514-07EE411F-D3E8-469E-B113-C034576EDF48
BestRank
Statement
http://www.wikidata.org/entity/statement/Q30496514-07EE411F-D3E8-469E-B113-C034576EDF48
Liver-directed recombinant adeno-associated viral gene delivery rescues a lethal mouse model of methylmalonic acidemia and provides long-term phenotypic correction
P2860
Q30496514-07EE411F-D3E8-469E-B113-C034576EDF48
BestRank
Statement
http://www.wikidata.org/entity/statement/Q30496514-07EE411F-D3E8-469E-B113-C034576EDF48
rank
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Statement
wasDerivedFrom
c05ddc65b352678f4d4086c84e6465ec07c198a8
P2860
Clinical outcome of long-term management of patients with vitamin B12-unresponsive methylmalonic acidemia.