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Q30574131-6BF6A81D-9838-4E2F-99E8-93B62132C6CC
Q30574131-6BF6A81D-9838-4E2F-99E8-93B62132C6CC
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http://www.wikidata.org/entity/statement/Q30574131-6BF6A81D-9838-4E2F-99E8-93B62132C6CC
Partial correction of the CNS lysosomal storage defect in a mouse model of juvenile neuronal ceroid lipofuscinosis by neonatal CNS administration of an adeno-associated virus serotype rh.10 vector expressing the human CLN3 gene.
P2860
Q30574131-6BF6A81D-9838-4E2F-99E8-93B62132C6CC
BestRank
Statement
http://www.wikidata.org/entity/statement/Q30574131-6BF6A81D-9838-4E2F-99E8-93B62132C6CC
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wasDerivedFrom
a6014e8fa7406677b097d2799475f1a021e326c6
P2860
Membrane trafficking and mitochondrial abnormalities precede subunit c deposition in a cerebellar cell model of juvenile neuronal ceroid lipofuscinosis