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Q30574131-7F624443-B0FA-4C06-B99A-9255A20C5BBF
Q30574131-7F624443-B0FA-4C06-B99A-9255A20C5BBF
BestRank
Statement
http://www.wikidata.org/entity/statement/Q30574131-7F624443-B0FA-4C06-B99A-9255A20C5BBF
Partial correction of the CNS lysosomal storage defect in a mouse model of juvenile neuronal ceroid lipofuscinosis by neonatal CNS administration of an adeno-associated virus serotype rh.10 vector expressing the human CLN3 gene.
P2860
Q30574131-7F624443-B0FA-4C06-B99A-9255A20C5BBF
BestRank
Statement
http://www.wikidata.org/entity/statement/Q30574131-7F624443-B0FA-4C06-B99A-9255A20C5BBF
rank
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type
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wasDerivedFrom
a6014e8fa7406677b097d2799475f1a021e326c6
P2860
Extended normal life after AAVrh10-mediated gene therapy in the mouse model of Krabbe disease.