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Q33635326-2A3C9FBC-71CB-41BB-B7E4-CF9685A4ACF4
Q33635326-2A3C9FBC-71CB-41BB-B7E4-CF9685A4ACF4
BestRank
Statement
http://www.wikidata.org/entity/statement/Q33635326-2A3C9FBC-71CB-41BB-B7E4-CF9685A4ACF4
Efficient SMN Rescue following Subcutaneous Tricyclo-DNA Antisense Oligonucleotide Treatment
P2860
Q33635326-2A3C9FBC-71CB-41BB-B7E4-CF9685A4ACF4
BestRank
Statement
http://www.wikidata.org/entity/statement/Q33635326-2A3C9FBC-71CB-41BB-B7E4-CF9685A4ACF4
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wasDerivedFrom
64f22757802b51d99c698e87285f062925aea3c5
P2860
Systemic peptide-mediated oligonucleotide therapy improves long-term survival in spinal muscular atrophy.