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Q33720730-828E831E-DC7C-412C-9CE0-4E59B7638C1A
Q33720730-828E831E-DC7C-412C-9CE0-4E59B7638C1A
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Statement
http://www.wikidata.org/entity/statement/Q33720730-828E831E-DC7C-412C-9CE0-4E59B7638C1A
Trans-splicing-mediated improvement in a severe mouse model of spinal muscular atrophy.
P2860
Q33720730-828E831E-DC7C-412C-9CE0-4E59B7638C1A
BestRank
Statement
http://www.wikidata.org/entity/statement/Q33720730-828E831E-DC7C-412C-9CE0-4E59B7638C1A
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wasDerivedFrom
00d2f238f577d8d1f378b4d7fa937f27c81d0ef2
P2860
A short antisense oligonucleotide masking a unique intronic motif prevents skipping of a critical exon in spinal muscular atrophy