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Q33871311-285B322C-9A29-4CA1-BB59-3250CF4F6F80
Q33871311-285B322C-9A29-4CA1-BB59-3250CF4F6F80
BestRank
Statement
http://www.wikidata.org/entity/statement/Q33871311-285B322C-9A29-4CA1-BB59-3250CF4F6F80
Spinal muscular atrophy: mechanisms and therapeutic strategies.
P2860
Q33871311-285B322C-9A29-4CA1-BB59-3250CF4F6F80
BestRank
Statement
http://www.wikidata.org/entity/statement/Q33871311-285B322C-9A29-4CA1-BB59-3250CF4F6F80
rank
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wasDerivedFrom
ac6e6a3df2951b5888be0944e751540c7fc90205
P2860
A short antisense oligonucleotide masking a unique intronic motif prevents skipping of a critical exon in spinal muscular atrophy