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Q34161415-4B3150FB-019A-45B9-BA82-E6792BCD63A9
Q34161415-4B3150FB-019A-45B9-BA82-E6792BCD63A9
BestRank
Statement
http://www.wikidata.org/entity/statement/Q34161415-4B3150FB-019A-45B9-BA82-E6792BCD63A9
Long-term systemic therapy of Fabry disease in a knockout mouse by adeno-associated virus-mediated muscle-directed gene transfer.
P2860
Q34161415-4B3150FB-019A-45B9-BA82-E6792BCD63A9
BestRank
Statement
http://www.wikidata.org/entity/statement/Q34161415-4B3150FB-019A-45B9-BA82-E6792BCD63A9
rank
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Statement
wasDerivedFrom
329f4fbd37398cf7bdf5916a35bf791b2b07385c
P2860
Fabry disease: preclinical studies demonstrate the effectiveness of alpha-galactosidase A replacement in enzyme-deficient mice.