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Q34171630-573534E5-08A3-4F93-AC1F-85FE9A303831
Q34171630-573534E5-08A3-4F93-AC1F-85FE9A303831
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http://www.wikidata.org/entity/statement/Q34171630-573534E5-08A3-4F93-AC1F-85FE9A303831
Optimizing exon skipping therapies for DMD.
P2860
Q34171630-573534E5-08A3-4F93-AC1F-85FE9A303831
BestRank
Statement
http://www.wikidata.org/entity/statement/Q34171630-573534E5-08A3-4F93-AC1F-85FE9A303831
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wasDerivedFrom
920bcde19aba775d3ceadad9dec0db0f8c8cac46
P2860
Characteristic mRNA abnormality found in half the patients with severe haemophilia A is due to large DNA inversions.