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Q34313390-B1FF7814-17CD-4DF7-BE3F-12D7DAE2BD29
Q34313390-B1FF7814-17CD-4DF7-BE3F-12D7DAE2BD29
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http://www.wikidata.org/entity/statement/Q34313390-B1FF7814-17CD-4DF7-BE3F-12D7DAE2BD29
Safety and pharmacodynamic effects of a pharmacological chaperone on α-galactosidase A activity and globotriaosylceramide clearance in Fabry disease: report from two phase 2 clinical studies.
P2860
Q34313390-B1FF7814-17CD-4DF7-BE3F-12D7DAE2BD29
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Statement
http://www.wikidata.org/entity/statement/Q34313390-B1FF7814-17CD-4DF7-BE3F-12D7DAE2BD29
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wasDerivedFrom
7c478f8f2db348408f0d0bf0966cf067494372f2
P2860
The pharmacological chaperone 1-deoxygalactonojirimycin increases alpha-galactosidase A levels in Fabry patient cell lines.