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Q34362524-0DAE4E68-C19E-4234-892D-99732BD62681
Q34362524-0DAE4E68-C19E-4234-892D-99732BD62681
BestRank
Statement
http://www.wikidata.org/entity/statement/Q34362524-0DAE4E68-C19E-4234-892D-99732BD62681
VX-809 corrects folding defects in cystic fibrosis transmembrane conductance regulator protein through action on membrane-spanning domain 1.
P2860
Q34362524-0DAE4E68-C19E-4234-892D-99732BD62681
BestRank
Statement
http://www.wikidata.org/entity/statement/Q34362524-0DAE4E68-C19E-4234-892D-99732BD62681
rank
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Statement
wasDerivedFrom
c707c9cf8b48600a7807059f897e6556f704154f
P2860
Results of a phase IIa study of VX-809, an investigational CFTR corrector compound, in subjects with cystic fibrosis homozygous for the F508del-CFTR mutation.