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Q34362524-5646D268-5C34-44A0-9102-E4B54DEB99AF
Q34362524-5646D268-5C34-44A0-9102-E4B54DEB99AF
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http://www.wikidata.org/entity/statement/Q34362524-5646D268-5C34-44A0-9102-E4B54DEB99AF
VX-809 corrects folding defects in cystic fibrosis transmembrane conductance regulator protein through action on membrane-spanning domain 1.
P2860
Q34362524-5646D268-5C34-44A0-9102-E4B54DEB99AF
BestRank
Statement
http://www.wikidata.org/entity/statement/Q34362524-5646D268-5C34-44A0-9102-E4B54DEB99AF
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wasDerivedFrom
c707c9cf8b48600a7807059f897e6556f704154f
P2860
Integrated biophysical studies implicate partial unfolding of NBD1 of CFTR in the molecular pathogenesis of F508del cystic fibrosis.