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Q34545883-7439208E-C846-4942-927E-2E969F227374
Q34545883-7439208E-C846-4942-927E-2E969F227374
BestRank
Statement
http://www.wikidata.org/entity/statement/Q34545883-7439208E-C846-4942-927E-2E969F227374
Therapies of mucopolysaccharidosis IVA (Morquio A syndrome).
P2860
Q34545883-7439208E-C846-4942-927E-2E969F227374
BestRank
Statement
http://www.wikidata.org/entity/statement/Q34545883-7439208E-C846-4942-927E-2E969F227374
rank
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type
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Statement
wasDerivedFrom
08b3922368acf8d990ce73cfc18be199e9425304
P2860
Direct gene transfer to the CNS prevents emergence of neurologic disease in a murine model of mucopolysaccharidosis type I.