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Q34555103-A9808F24-25D3-4BD2-8061-8558251B832B
Q34555103-A9808F24-25D3-4BD2-8061-8558251B832B
BestRank
Statement
http://www.wikidata.org/entity/statement/Q34555103-A9808F24-25D3-4BD2-8061-8558251B832B
ISS-N1 makes the First FDA-approved Drug for Spinal Muscular Atrophy.
P2860
Q34555103-A9808F24-25D3-4BD2-8061-8558251B832B
BestRank
Statement
http://www.wikidata.org/entity/statement/Q34555103-A9808F24-25D3-4BD2-8061-8558251B832B
rank
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wasDerivedFrom
f0381584c930fd76b9a47a4733aec2a86adba646
P2860
A novel morpholino oligomer targeting ISS-N1 improves rescue of severe spinal muscular atrophy transgenic mice