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Q34566454-2386F105-1FFA-4E60-A1E7-249C16792CB6
Q34566454-2386F105-1FFA-4E60-A1E7-249C16792CB6
BestRank
Statement
http://www.wikidata.org/entity/statement/Q34566454-2386F105-1FFA-4E60-A1E7-249C16792CB6
Gene replacement therapies for duchenne muscular dystrophy using adeno-associated viral vectors.
P2860
Q34566454-2386F105-1FFA-4E60-A1E7-249C16792CB6
BestRank
Statement
http://www.wikidata.org/entity/statement/Q34566454-2386F105-1FFA-4E60-A1E7-249C16792CB6
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wasDerivedFrom
d25fc032782d8a75d545b908f2ded7a822cc924a
P2860
Widespread muscle expression of an AAV9 human mini-dystrophin vector after intravenous injection in neonatal dystrophin-deficient dogs.