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Q34633246-68BD9617-73C1-4422-BD99-433380E393A4
Q34633246-68BD9617-73C1-4422-BD99-433380E393A4
BestRank
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http://www.wikidata.org/entity/statement/Q34633246-68BD9617-73C1-4422-BD99-433380E393A4
Enzyme replacement therapy in newborn mucopolysaccharidosis IVA mice: early treatment rescues bone lesions?
P2860
Q34633246-68BD9617-73C1-4422-BD99-433380E393A4
BestRank
Statement
http://www.wikidata.org/entity/statement/Q34633246-68BD9617-73C1-4422-BD99-433380E393A4
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2c27429302bdfd56932020a5b270f3bb90eaac5e
P2860
A phase II/III clinical study of enzyme replacement therapy with idursulfase in mucopolysaccharidosis II (Hunter syndrome)