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Q34633598-5CA43F4B-50CD-459E-8715-6A44AD8577FF
Q34633598-5CA43F4B-50CD-459E-8715-6A44AD8577FF
BestRank
Statement
http://www.wikidata.org/entity/statement/Q34633598-5CA43F4B-50CD-459E-8715-6A44AD8577FF
Phase 1 gene therapy for Duchenne muscular dystrophy using a translational optimized AAV vector.
P2860
Q34633598-5CA43F4B-50CD-459E-8715-6A44AD8577FF
BestRank
Statement
http://www.wikidata.org/entity/statement/Q34633598-5CA43F4B-50CD-459E-8715-6A44AD8577FF
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wasDerivedFrom
1ebc25bcf76a04f232f6ca4fd3e44136a537d39e
P2860
Mutations on the external surfaces of adeno-associated virus type 2 capsids that affect transduction and neutralization.