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Q34695728-134E5CA4-38FF-4689-8749-A4D22B303296
Q34695728-134E5CA4-38FF-4689-8749-A4D22B303296
BestRank
Statement
http://www.wikidata.org/entity/statement/Q34695728-134E5CA4-38FF-4689-8749-A4D22B303296
Improved antisense oligonucleotide design to suppress aberrant SMN2 gene transcript processing: towards a treatment for spinal muscular atrophy
P2860
Q34695728-134E5CA4-38FF-4689-8749-A4D22B303296
BestRank
Statement
http://www.wikidata.org/entity/statement/Q34695728-134E5CA4-38FF-4689-8749-A4D22B303296
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Statement
wasDerivedFrom
e65edda4884415fd0058021402c4bf386156f7cf
P2860
Systemic delivery of scAAV9 expressing SMN prolongs survival in a model of spinal muscular atrophy.