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Q34762623-1B9763EC-741A-4FB0-9D3E-FE50E3109365
Q34762623-1B9763EC-741A-4FB0-9D3E-FE50E3109365
BestRank
Statement
http://www.wikidata.org/entity/statement/Q34762623-1B9763EC-741A-4FB0-9D3E-FE50E3109365
Repair of pre-mRNA splicing: prospects for a therapy for spinal muscular atrophy.
P2860
Q34762623-1B9763EC-741A-4FB0-9D3E-FE50E3109365
BestRank
Statement
http://www.wikidata.org/entity/statement/Q34762623-1B9763EC-741A-4FB0-9D3E-FE50E3109365
rank
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Statement
wasDerivedFrom
1417dbdc674e410ddf0e3e7dbc7db7a49075ce7b
P2860
A short antisense oligonucleotide masking a unique intronic motif prevents skipping of a critical exon in spinal muscular atrophy