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Q34883011-3FB643A1-100C-47C8-9306-7596D23A3AE5
Q34883011-3FB643A1-100C-47C8-9306-7596D23A3AE5
BestRank
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http://www.wikidata.org/entity/statement/Q34883011-3FB643A1-100C-47C8-9306-7596D23A3AE5
Bi-specific splice-switching PMO oligonucleotides conjugated via a single peptide active in a mouse model of Duchenne muscular dystrophy.
P2860
Q34883011-3FB643A1-100C-47C8-9306-7596D23A3AE5
BestRank
Statement
http://www.wikidata.org/entity/statement/Q34883011-3FB643A1-100C-47C8-9306-7596D23A3AE5
rank
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type
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wasDerivedFrom
6ac716182167860c9d889a719176576e2691f3d4
P2860
Eteplirsen for the treatment of Duchenne muscular dystrophy.