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Q34985915-91FC58B0-BCEA-4641-95D7-A7F3C400B4C0
Q34985915-91FC58B0-BCEA-4641-95D7-A7F3C400B4C0
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http://www.wikidata.org/entity/statement/Q34985915-91FC58B0-BCEA-4641-95D7-A7F3C400B4C0
Novel LIPA mutations in Mexican siblings with lysosomal acid lipase deficiency
P2860
Q34985915-91FC58B0-BCEA-4641-95D7-A7F3C400B4C0
BestRank
Statement
http://www.wikidata.org/entity/statement/Q34985915-91FC58B0-BCEA-4641-95D7-A7F3C400B4C0
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7301648e046631c6d1b5724c471810afe4e733fc
P2860
Sebelipase alfa over 52 weeks reduces serum transaminases, liver volume and improves serum lipids in patients with lysosomal acid lipase deficiency.