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1
Q35056076-408FEBB9-2EE0-464C-B33A-1218FBBAB7D3
Q35056076-408FEBB9-2EE0-464C-B33A-1218FBBAB7D3
BestRank
Statement
http://www.wikidata.org/entity/statement/Q35056076-408FEBB9-2EE0-464C-B33A-1218FBBAB7D3
Substrate reduction therapy: miglustat as a remedy for symptomatic patients with Gaucher disease type 1.
P2860
Q35056076-408FEBB9-2EE0-464C-B33A-1218FBBAB7D3
BestRank
Statement
http://www.wikidata.org/entity/statement/Q35056076-408FEBB9-2EE0-464C-B33A-1218FBBAB7D3
rank
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Statement
wasDerivedFrom
d0455cebd71aaa6525eb69540a2796fb1a0a37e8
P2860
New therapeutic prospects for the glycosphingolipid lysosomal storage diseases.