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Q35056714-025326DF-B3B0-4767-9279-55D00B42B63D
Q35056714-025326DF-B3B0-4767-9279-55D00B42B63D
BestRank
Statement
http://www.wikidata.org/entity/statement/Q35056714-025326DF-B3B0-4767-9279-55D00B42B63D
Vector design influences hepatic genotoxicity after adeno-associated virus gene therapy.
P2860
Q35056714-025326DF-B3B0-4767-9279-55D00B42B63D
BestRank
Statement
http://www.wikidata.org/entity/statement/Q35056714-025326DF-B3B0-4767-9279-55D00B42B63D
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wasDerivedFrom
4565fe7358fbae84da7989d1770891135f919ec5
P2860
Liver-directed recombinant adeno-associated viral gene delivery rescues a lethal mouse model of methylmalonic acidemia and provides long-term phenotypic correction