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Q35078437-A2BAC621-A9AF-4A0A-ACE5-332368AAB330
Q35078437-A2BAC621-A9AF-4A0A-ACE5-332368AAB330
BestRank
Statement
http://www.wikidata.org/entity/statement/Q35078437-A2BAC621-A9AF-4A0A-ACE5-332368AAB330
Employing a gain-of-function factor IX variant R338L to advance the efficacy and safety of hemophilia B human gene therapy: preclinical evaluation supporting an ongoing adeno-associated virus clinical trial.
P2860
Q35078437-A2BAC621-A9AF-4A0A-ACE5-332368AAB330
BestRank
Statement
http://www.wikidata.org/entity/statement/Q35078437-A2BAC621-A9AF-4A0A-ACE5-332368AAB330
rank
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type
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Statement
wasDerivedFrom
ac56e9220d8ac9b3edb683be7373d8353b4b582d
P2860
Abnormal hemostasis in a knock-in mouse carrying a variant of factor IX with impaired binding to collagen type IV.