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Q36134910-09BE305A-AB27-432E-B480-590539349C08
Q36134910-09BE305A-AB27-432E-B480-590539349C08
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Statement
http://www.wikidata.org/entity/statement/Q36134910-09BE305A-AB27-432E-B480-590539349C08
Early treatment with laronidase improves clinical outcomes in patients with attenuated MPS I: a retrospective case series analysis of nine sibships.
P2860
Q36134910-09BE305A-AB27-432E-B480-590539349C08
BestRank
Statement
http://www.wikidata.org/entity/statement/Q36134910-09BE305A-AB27-432E-B480-590539349C08
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wasDerivedFrom
4209e350e9ae135f1052b1ea923748e37de2fa9d
P2860
Anthropometric data of 14 patients with mucopolysaccharidosis I: retrospective analysis and efficacy of recombinant human alpha-L-iduronidase (laronidase).