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Q36164927-70B28E7C-0981-4E82-B811-BF0FCE5C9B97
Q36164927-70B28E7C-0981-4E82-B811-BF0FCE5C9B97
BestRank
Statement
http://www.wikidata.org/entity/statement/Q36164927-70B28E7C-0981-4E82-B811-BF0FCE5C9B97
Evaluation of Readministration of a Recombinant Adeno-Associated Virus Vector Expressing Acid Alpha-Glucosidase in Pompe Disease: Preclinical to Clinical Planning.
P2860
Q36164927-70B28E7C-0981-4E82-B811-BF0FCE5C9B97
BestRank
Statement
http://www.wikidata.org/entity/statement/Q36164927-70B28E7C-0981-4E82-B811-BF0FCE5C9B97
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Statement
wasDerivedFrom
4c04364e1a83d0b11debef320912f51c848bbb51
P2860
Limb-girdle muscular dystrophy type 2D gene therapy restores alpha-sarcoglycan and associated proteins.