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Q36410390-23CF49E5-24DC-400A-A297-73A201E1AD1B
Q36410390-23CF49E5-24DC-400A-A297-73A201E1AD1B
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http://www.wikidata.org/entity/statement/Q36410390-23CF49E5-24DC-400A-A297-73A201E1AD1B
Chronic enzyme replacement therapy ameliorates neuropathology in alpha-mannosidosis mice
P2860
Q36410390-23CF49E5-24DC-400A-A297-73A201E1AD1B
BestRank
Statement
http://www.wikidata.org/entity/statement/Q36410390-23CF49E5-24DC-400A-A297-73A201E1AD1B
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e3ce709f9ecc5c40a82120b4f8adbdb994cdc138
P2860
Intravenous high-dose enzyme replacement therapy with recombinant palmitoyl-protein thioesterase reduces visceral lysosomal storage and modestly prolongs survival in a preclinical mouse model of infantile neuronal ceroid lipofuscinosis.