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Q36482816-CB18B8C4-2E05-406B-B22A-A794994BF35B
Q36482816-CB18B8C4-2E05-406B-B22A-A794994BF35B
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http://www.wikidata.org/entity/statement/Q36482816-CB18B8C4-2E05-406B-B22A-A794994BF35B
AAV-mediated gene delivery in a feline model of Sandhoff disease corrects lysosomal storage in the central nervous system.
P2860
Q36482816-CB18B8C4-2E05-406B-B22A-A794994BF35B
BestRank
Statement
http://www.wikidata.org/entity/statement/Q36482816-CB18B8C4-2E05-406B-B22A-A794994BF35B
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3eaf8f97cf3eed2bee3765ac8b83227f1bf0489d
P2860
Reversibility of neuropathology in Tay-Sachs-related diseases.