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Q36676838-593C661A-048F-47B7-8035-C16F7634492B
Q36676838-593C661A-048F-47B7-8035-C16F7634492B
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http://www.wikidata.org/entity/statement/Q36676838-593C661A-048F-47B7-8035-C16F7634492B
Genetic and pharmacological evidence implicates cathepsins in Niemann-Pick C cerebellar degeneration.
P2860
Q36676838-593C661A-048F-47B7-8035-C16F7634492B
BestRank
Statement
http://www.wikidata.org/entity/statement/Q36676838-593C661A-048F-47B7-8035-C16F7634492B
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400dfd247c09d244ab2d94d25f5a1db68850f868
P2860
Ryanodine receptor antagonists adapt NPC1 proteostasis to ameliorate lipid storage in Niemann-Pick type C disease fibroblasts