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Q36822452-F810CCC0-4397-4650-9733-571C9A4EEFCE
Q36822452-F810CCC0-4397-4650-9733-571C9A4EEFCE
BestRank
Statement
http://www.wikidata.org/entity/statement/Q36822452-F810CCC0-4397-4650-9733-571C9A4EEFCE
Novel therapeutic targets for the treatment of Fabry disease.
P2860
Q36822452-F810CCC0-4397-4650-9733-571C9A4EEFCE
BestRank
Statement
http://www.wikidata.org/entity/statement/Q36822452-F810CCC0-4397-4650-9733-571C9A4EEFCE
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59d8b7b6149183dccbf2bc25172a39b9ec93bac7
P2860
Pharmacological chaperone corrects lysosomal storage in Fabry disease caused by trafficking-incompetent variants.