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Q37127561-04424E00-8597-41C3-B893-787B65A6978A
Q37127561-04424E00-8597-41C3-B893-787B65A6978A
BestRank
Statement
http://www.wikidata.org/entity/statement/Q37127561-04424E00-8597-41C3-B893-787B65A6978A
Therapeutic advances in the management of Pompe disease and other metabolic myopathies
P2860
Q37127561-04424E00-8597-41C3-B893-787B65A6978A
BestRank
Statement
http://www.wikidata.org/entity/statement/Q37127561-04424E00-8597-41C3-B893-787B65A6978A
rank
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Statement
wasDerivedFrom
73f4526ef11ab15ab584476e251d6c50bd74c546
P2860
Observational clinical study in juvenile-adult glycogenosis type 2 patients undergoing enzyme replacement therapy for up to 4 years.