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Q37358381-0A7C5F7E-48ED-49D6-A5A3-F286522F88B3
Q37358381-0A7C5F7E-48ED-49D6-A5A3-F286522F88B3
BestRank
Statement
http://www.wikidata.org/entity/statement/Q37358381-0A7C5F7E-48ED-49D6-A5A3-F286522F88B3
Long-term expression and safety of administration of AAVrh.10hCLN2 to the brain of rats and nonhuman primates for the treatment of late infantile neuronal ceroid lipofuscinosis.
P2860
Q37358381-0A7C5F7E-48ED-49D6-A5A3-F286522F88B3
BestRank
Statement
http://www.wikidata.org/entity/statement/Q37358381-0A7C5F7E-48ED-49D6-A5A3-F286522F88B3
rank
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wasDerivedFrom
27ea897d37835941786d13498de340372e4009dd
P2860
Mutational analysis of the defective protease in classic late-infantile neuronal ceroid lipofuscinosis, a neurodegenerative lysosomal storage disorder