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Q37369090-08FCBB70-489B-446D-B282-8D465A9A58C7
Q37369090-08FCBB70-489B-446D-B282-8D465A9A58C7
BestRank
Statement
http://www.wikidata.org/entity/statement/Q37369090-08FCBB70-489B-446D-B282-8D465A9A58C7
CRISPR RNA-guided FokI nucleases repair a PAH variant in a phenylketonuria model.
P2860
Q37369090-08FCBB70-489B-446D-B282-8D465A9A58C7
BestRank
Statement
http://www.wikidata.org/entity/statement/Q37369090-08FCBB70-489B-446D-B282-8D465A9A58C7
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Statement
wasDerivedFrom
9dac1b0ecee7682bc09d9c29a6c9bb8452876fca
P2860
Seamless gene correction of β-thalassemia mutations in patient-specific iPSCs using CRISPR/Cas9 and piggyBac.