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Q37609948-113BBC58-E847-4611-9637-85568430D8ED
Q37609948-113BBC58-E847-4611-9637-85568430D8ED
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http://www.wikidata.org/entity/statement/Q37609948-113BBC58-E847-4611-9637-85568430D8ED
Progress in therapeutic antisense applications for neuromuscular disorders.
P2860
Q37609948-113BBC58-E847-4611-9637-85568430D8ED
BestRank
Statement
http://www.wikidata.org/entity/statement/Q37609948-113BBC58-E847-4611-9637-85568430D8ED
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31524f7bed7ac841fd9032b52cde2cd1cd1167f6
P2860
A single nucleotide in the SMN gene regulates splicing and is responsible for spinal muscular atrophy