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Q37695999-8784732F-715A-48D9-867E-C55915DEE917
Q37695999-8784732F-715A-48D9-867E-C55915DEE917
BestRank
Statement
http://www.wikidata.org/entity/statement/Q37695999-8784732F-715A-48D9-867E-C55915DEE917
Systemic delivery of factor IX messenger RNA for protein replacement therapy
P2860
Q37695999-8784732F-715A-48D9-867E-C55915DEE917
BestRank
Statement
http://www.wikidata.org/entity/statement/Q37695999-8784732F-715A-48D9-867E-C55915DEE917
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wasDerivedFrom
ab88c961e0e16ec70ef791ac6da0b96753ae1894
P2860
Efficacy and safety of patisiran for familial amyloidotic polyneuropathy: a phase II multi-dose study