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1
Q37726532-707F6E40-4768-4A41-869F-E86518B9637D
Q37726532-707F6E40-4768-4A41-869F-E86518B9637D
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Statement
http://www.wikidata.org/entity/statement/Q37726532-707F6E40-4768-4A41-869F-E86518B9637D
Nonsense Suppression as an Approach to Treat Lysosomal Storage Diseases.
P2860
Q37726532-707F6E40-4768-4A41-869F-E86518B9637D
BestRank
Statement
http://www.wikidata.org/entity/statement/Q37726532-707F6E40-4768-4A41-869F-E86518B9637D
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Statement
wasDerivedFrom
3eab25222d8ce44b95bc9a43f59dfecee35f20c5
P2860
PTC124 targets genetic disorders caused by nonsense mutations.