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Q38195295-0C5C05DC-07E3-4F35-BC45-F11AA6EC935F
Q38195295-0C5C05DC-07E3-4F35-BC45-F11AA6EC935F
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http://www.wikidata.org/entity/statement/Q38195295-0C5C05DC-07E3-4F35-BC45-F11AA6EC935F
New developments in exon skipping and splice modulation therapies for neuromuscular diseases.
P2860
Q38195295-0C5C05DC-07E3-4F35-BC45-F11AA6EC935F
BestRank
Statement
http://www.wikidata.org/entity/statement/Q38195295-0C5C05DC-07E3-4F35-BC45-F11AA6EC935F
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d72bbd37fc24225b9ca6839a18df54adb6a66749
P2860
Restoration of correct splicing in thalassemic pre-mRNA by antisense oligonucleotides