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Q38424066-517553BF-EEB5-4409-892F-71DBEEC15613
Q38424066-517553BF-EEB5-4409-892F-71DBEEC15613
BestRank
Statement
http://www.wikidata.org/entity/statement/Q38424066-517553BF-EEB5-4409-892F-71DBEEC15613
Pharmacological Chaperone Therapy: Preclinical Development, Clinical Translation, and Prospects for the Treatment of Lysosomal Storage Disorders.
P2860
Q38424066-517553BF-EEB5-4409-892F-71DBEEC15613
BestRank
Statement
http://www.wikidata.org/entity/statement/Q38424066-517553BF-EEB5-4409-892F-71DBEEC15613
rank
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wasDerivedFrom
77dbee361d3203b1f52d9465b4c23ef2f3965400
P2860
Pharmacological chaperone corrects lysosomal storage in Fabry disease caused by trafficking-incompetent variants.