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Q38489298-D36E7FF6-51B2-4F7E-A046-B3AF2919431D
Q38489298-D36E7FF6-51B2-4F7E-A046-B3AF2919431D
BestRank
Statement
http://www.wikidata.org/entity/statement/Q38489298-D36E7FF6-51B2-4F7E-A046-B3AF2919431D
Spinal muscular atrophy--recent therapeutic advances for an old challenge.
P2860
Q38489298-D36E7FF6-51B2-4F7E-A046-B3AF2919431D
BestRank
Statement
http://www.wikidata.org/entity/statement/Q38489298-D36E7FF6-51B2-4F7E-A046-B3AF2919431D
rank
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wasDerivedFrom
6d721393297e00bd26b228289eafc788d48841e4
P2860
A novel morpholino oligomer targeting ISS-N1 improves rescue of severe spinal muscular atrophy transgenic mice