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Q38546908-DE9FB82C-B9E9-46AE-8408-626ED06364CD
Q38546908-DE9FB82C-B9E9-46AE-8408-626ED06364CD
BestRank
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http://www.wikidata.org/entity/statement/Q38546908-DE9FB82C-B9E9-46AE-8408-626ED06364CD
Developing therapies for spinal muscular atrophy.
P2860
Q38546908-DE9FB82C-B9E9-46AE-8408-626ED06364CD
BestRank
Statement
http://www.wikidata.org/entity/statement/Q38546908-DE9FB82C-B9E9-46AE-8408-626ED06364CD
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f197c7de29427e5c8cbb60deb8012457f61ef12e
P2860
New developments in exon skipping and splice modulation therapies for neuromuscular diseases.