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Q38685408-6EF46001-9210-4805-96D0-D9EB72138030
Q38685408-6EF46001-9210-4805-96D0-D9EB72138030
BestRank
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http://www.wikidata.org/entity/statement/Q38685408-6EF46001-9210-4805-96D0-D9EB72138030
Longitudinal characterization of biomarkers for spinal muscular atrophy.
P2860
Q38685408-6EF46001-9210-4805-96D0-D9EB72138030
BestRank
Statement
http://www.wikidata.org/entity/statement/Q38685408-6EF46001-9210-4805-96D0-D9EB72138030
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014238998f6a9a6b9025cb6e4c56e60b2b65d5f1
P2860
New developments in exon skipping and splice modulation therapies for neuromuscular diseases.