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Q38696285-03D5116E-9ED5-4F15-8A38-83746224ADC1
Q38696285-03D5116E-9ED5-4F15-8A38-83746224ADC1
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Statement
http://www.wikidata.org/entity/statement/Q38696285-03D5116E-9ED5-4F15-8A38-83746224ADC1
Current Progress in Therapeutic Gene Editing for Monogenic Diseases
P2860
Q38696285-03D5116E-9ED5-4F15-8A38-83746224ADC1
BestRank
Statement
http://www.wikidata.org/entity/statement/Q38696285-03D5116E-9ED5-4F15-8A38-83746224ADC1
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wasDerivedFrom
574192fff1616bb206e9a8090ab5f8ed8aab40e9
P2860
Cystic fibrosis transmembrane conductance regulator (CFTR) potentiator VX-770 (ivacaftor) opens the defective channel gate of mutant CFTR in a phosphorylation-dependent but ATP-independent manner.