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1
Q38734734-0A59408C-241D-4F7D-96BE-10E4569B9FA6
Q38734734-0A59408C-241D-4F7D-96BE-10E4569B9FA6
BestRank
Statement
http://www.wikidata.org/entity/statement/Q38734734-0A59408C-241D-4F7D-96BE-10E4569B9FA6
Antisense Oligonucleotide-Based Therapy for Neuromuscular Disease.
P2860
Q38734734-0A59408C-241D-4F7D-96BE-10E4569B9FA6
BestRank
Statement
http://www.wikidata.org/entity/statement/Q38734734-0A59408C-241D-4F7D-96BE-10E4569B9FA6
rank
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Statement
wasDerivedFrom
aad3a463db94089aa0ce1661b03761b5352fb61a
P2860
Results from a phase 1 study of nusinersen (ISIS-SMN(Rx)) in children with spinal muscular atrophy.