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Q39028972-47E33DF4-908D-4DC2-9FDE-8A62A5BB39FC
Q39028972-47E33DF4-908D-4DC2-9FDE-8A62A5BB39FC
BestRank
Statement
http://www.wikidata.org/entity/statement/Q39028972-47E33DF4-908D-4DC2-9FDE-8A62A5BB39FC
Gaucher disease: Progress and ongoing challenges.
P2860
Q39028972-47E33DF4-908D-4DC2-9FDE-8A62A5BB39FC
BestRank
Statement
http://www.wikidata.org/entity/statement/Q39028972-47E33DF4-908D-4DC2-9FDE-8A62A5BB39FC
rank
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Statement
wasDerivedFrom
662f1d7a44b2f150a52151671592866f47f918d3
P2860
A phase 2 study of eliglustat tartrate (Genz-112638), an oral substrate reduction therapy for Gaucher disease type 1.