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Q39337972-52A4020C-813F-40C2-A45A-7A1C13B82DD2
Q39337972-52A4020C-813F-40C2-A45A-7A1C13B82DD2
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http://www.wikidata.org/entity/statement/Q39337972-52A4020C-813F-40C2-A45A-7A1C13B82DD2
Developmental regulation of SMN expression: pathophysiological implications and perspectives for therapy development in spinal muscular atrophy.
P2860
Q39337972-52A4020C-813F-40C2-A45A-7A1C13B82DD2
BestRank
Statement
http://www.wikidata.org/entity/statement/Q39337972-52A4020C-813F-40C2-A45A-7A1C13B82DD2
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fddc19faac588c73fd0c99c6d4dc9a35d42ce8d3
P2860
A single administration of morpholino antisense oligomer rescues spinal muscular atrophy in mouse