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Q39350652-2447A5A0-CB11-46A7-8D72-9D54A37A2679
Q39350652-2447A5A0-CB11-46A7-8D72-9D54A37A2679
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http://www.wikidata.org/entity/statement/Q39350652-2447A5A0-CB11-46A7-8D72-9D54A37A2679
A novel morpholino oligomer targeting ISS-N1 improves rescue of severe spinal muscular atrophy transgenic mice
P2860
Q39350652-2447A5A0-CB11-46A7-8D72-9D54A37A2679
BestRank
Statement
http://www.wikidata.org/entity/statement/Q39350652-2447A5A0-CB11-46A7-8D72-9D54A37A2679
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wasDerivedFrom
835deb128a20508a509a41b7a0cfbdba8d5710a3
P2860
Neuronal SMN expression corrects spinal muscular atrophy in severe SMA mice while muscle-specific SMN expression has no phenotypic effect.