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Q39350652-2BC6B2A1-E2F1-4454-8AC0-E20EDB735368
Q39350652-2BC6B2A1-E2F1-4454-8AC0-E20EDB735368
BestRank
Statement
http://www.wikidata.org/entity/statement/Q39350652-2BC6B2A1-E2F1-4454-8AC0-E20EDB735368
A novel morpholino oligomer targeting ISS-N1 improves rescue of severe spinal muscular atrophy transgenic mice
P2860
Q39350652-2BC6B2A1-E2F1-4454-8AC0-E20EDB735368
BestRank
Statement
http://www.wikidata.org/entity/statement/Q39350652-2BC6B2A1-E2F1-4454-8AC0-E20EDB735368
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wasDerivedFrom
03e76b1dddcc32ca2cbaf7228b3242e503e3686b
P2860
Mipomersen, an apolipoprotein B synthesis inhibitor, for lowering of LDL cholesterol concentrations in patients with homozygous familial hypercholesterolaemia: a randomised, double-blind, placebo-controlled trial.