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Q39350652-38ED0F0D-9D58-44F0-8B9F-BA40A806E01D
Q39350652-38ED0F0D-9D58-44F0-8B9F-BA40A806E01D
BestRank
Statement
http://www.wikidata.org/entity/statement/Q39350652-38ED0F0D-9D58-44F0-8B9F-BA40A806E01D
A novel morpholino oligomer targeting ISS-N1 improves rescue of severe spinal muscular atrophy transgenic mice
P2860
Q39350652-38ED0F0D-9D58-44F0-8B9F-BA40A806E01D
BestRank
Statement
http://www.wikidata.org/entity/statement/Q39350652-38ED0F0D-9D58-44F0-8B9F-BA40A806E01D
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wasDerivedFrom
835deb128a20508a509a41b7a0cfbdba8d5710a3
P2860
Restoration of correct splicing in thalassemic pre-mRNA by antisense oligonucleotides